Medications for Glycogen Storage Disease Type Ii

3 results

  • lumizyme - alglucosidase alfa injection, powder, for solution

    (Alglucosidase Alfa)
    Genzyme Corporation
    Lumizyme is indicated for patients with Pompe disease (acid alpha-glucosidase deficiency), a rare genetic condition affecting lysosomal glycogen breakdown.
    Medication Details

  • nexviazyme - avalglucosidase alfa - ngpt injection, powder, lyophilized, for solution

    (Avalglucosidase Alfa-Ngpt)
    Genzyme Corporation
    Nexviazyme treats late-onset Pompe disease (lysosomal acid alpha-glucosidase deficiency) in patients 1 year and older.
    Medication Details

  • pombiliti atga - cipaglucosidase alfa - atga injection, powder, lyophilized, for solution

    (Cipaglucosidase Alfa-Atga)
    Amicus Therapeutics Us, Llc
    Pombiliti, used with Opfolda, treats late-onset Pompe disease (GAA deficiency) in adults weighing ≥40 kg who are not improving on current enzyme replacement therapy.
    Medication Details