Medications for Fabry Disease

3 results
  • elfabrio - pegunigalsidase alfa injection, solution, concentrate

    (Pegunigalsidase Alfa)
    Chiesi Usa, Inc.
    Elfabrio is indicated for the treatment of adults with confirmed Fabry disease.
  • galafold - migalastat hydrochloride capsule

    (Migalastat Hydrochloride)
    Amicus Therapeutics Us, Llc
    Galafold treats adults with confirmed Fabry disease who have an amenable GLA gene variant, as determined by in vitro assay data. Approved under accelerated approval based on reduction of kidney substrate (KIC GL-3).