Medications for Ceroid Lipofuscinosis Neuronal 2

1 result
  • brineura - cerliponase alfa

    (Cerliponase Alfa)
    Biomarin Pharmaceutical Inc.
    Brineura slows the loss of walking ability in children with neuronal ceroid lipofuscinosis type 2 (CLN2 disease), a rare inherited disorder caused by TPP1 enzyme deficiency.