Medications for Amyloidosis Hereditary Transthyretinrelated

2 results
  • onpattro - patisiran injection, lipid complex

    (Patisiran)
    Alnylam Pharmaceuticals, Inc.
    Onpattro treats polyneuropathy caused by hereditary transthyretin-mediated amyloidosis in adults.
  • vyndaqel - tafamidis meglumine capsule, liquid filled

    (Tafamidis Meglumine)
    Pfizer Laboratories Div Pfizer Inc
    Vyndaqel treats cardiomyopathy caused by wild-type or hereditary transthyretin-mediated amyloidosis (ATTR-CM) in adults, reducing cardiovascular mortality and cardiovascular-related hospitalization.