Carbamoyl Phosphate Synthetase 1 Activator [EPC] class drugs

4 results
  • carbaglu - carglumic acid tablet, for suspension

    (Carglumic Acid)
    Recordati Rare Diseases
    Carbaglu treats acute and chronic hyperammonemia in adults and pediatric patients with N-acetylglutamate synthase (NAGS) deficiency as adjunctive or maintenance therapy, and acute hyperammonemia due to propionic acidemia or methylmalonic acidemia as adjunctive therapy to standard of care.